A Randomized, Parallel-arm, Double Blind, Placebo-controlled Study to Assess the Efficacy of Fampridine for Patients With Spinocerebellar Ataxia SCA27B Caused by a GAA Expansion in the FGF14 Gene - Join Clinical Trial NCTNCT07185347
How to Join This Clinical Trial - NCTNCT07185347
Learn how to participate in this PHASE3 trial studying an investigational therapy for Spinocerebellar Ataxia 27B (SCA27B). Current status: NOT_YET_RECRUITING.
Am I Eligible for This Clinical Trial?
This clinical research study is looking for participants with Spinocerebellar Ataxia 27B (SCA27B). Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.
- Condition Being Studied
- Spinocerebellar Ataxia 27B (SCA27B)
- Treatment Being Tested
- Investigational treatment
- Study Phase
- PHASE3 - Large-scale efficacy study
- Enrollment Status
- NOT_YET_RECRUITING
- Study Identifier
- NCTNCT07185347 - ClinicalTrials.gov Identifier
- Sponsored By
- Study sponsor
What to Expect as a Participant
Participating in this clinical trial involves:
- Initial screening to determine eligibility
- Regular study visits and health assessments
- Receiving the study treatment or placebo
- Medical monitoring and follow-up care
- Contributing to medical research that may help others
- Potential access to new treatments before they're widely available
Clinical Trial Benefits and Compensation
Participants in this clinical research study may receive:
- Close medical monitoring by healthcare professionals
- Access to potential new treatments
- Compensation for time and travel (varies by study)
- No-cost study-related medical care
- The opportunity to help advance medical knowledge
Where Is This Clinical Trial Located?
This study is enrolling participants at 9 locations. Find a study site near you:
Clinical Research Site
Angers, - France
Status: Contact for availability
Clinical Research Site
Bordeaux, - France
Status: Contact for availability
Clinical Research Site
Dijon, - France
Status: Contact for availability
Clinical Research Site
Lyon, - France
Status: Contact for availability
Clinical Research Site
Montpellier, - France
Status: Contact for availability
Clinical Research Site
Paris, - France
Status: Contact for availability
Clinical Research Site
Rouen, - France
Status: Contact for availability
Clinical Research Site
Strasbourg, - France
Status: Contact for availability
Clinical Research Site
Toulouse, - France
Status: Contact for availability
How to Enroll in This Study
To learn more about participating in this PHASE3 clinical trial for Spinocerebellar Ataxia 27B (SCA27B):
- Review the eligibility criteria with your healthcare provider
- Contact the study team for a pre-screening interview
- Schedule an in-person screening visit if eligible
- Review and sign the informed consent form
- Begin participation in the clinical trial
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