Patient Guide: A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC)

Why Use Quri.ai for This Trial?

  • ✓ Simplified eligibility checker - know if you qualify in minutes
  • ✓ Direct contact with study coordinators at 27 locations
  • ✓ Plain language explanations of medical terms and procedures
  • ✓ Personalized enrollment support throughout your journey
  • ✓ Free service - no hidden fees or obligations
Trial ID: NCTNCT07082725
Status: 🟢 Enrolling Now
Condition: Niemann-Pick Type C Disease
Phase: PHASE3

Where You Can Participate

This study is available at 27 locations across the country.

Top locations include:
  • • Oakland, California
  • • Fairfax, Virginia
  • • Ciudad Autónoma Buenos Aires, Buenos Aires
  • • And 24 more locations

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A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC) - Join Clinical Trial NCTNCT07082725

How to Join This Clinical Trial - NCTNCT07082725

Learn how to participate in this PHASE3 trial studying an investigational therapy for Niemann-Pick Type C Disease. This study is currently enrolling participants.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Niemann-Pick Type C Disease. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied
Niemann-Pick Type C Disease
Treatment Being Tested
Investigational treatment
Study Phase
PHASE3 - Large-scale efficacy study
Enrollment Status
Currently enrolling participants
Study Identifier
NCTNCT07082725 - ClinicalTrials.gov Identifier
Sponsored By
Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

  • Initial screening to determine eligibility
  • Regular study visits and health assessments
  • Receiving the study treatment or placebo
  • Medical monitoring and follow-up care
  • Contributing to medical research that may help others
  • Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

  • Close medical monitoring by healthcare professionals
  • Access to potential new treatments
  • Compensation for time and travel (varies by study)
  • No-cost study-related medical care
  • The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 27 locations. Find a study site near you:

Clinical Research Site

Oakland, California 94609 - United States

Status: NOT_YET_RECRUITING

Clinical Research Site

Fairfax, Virginia 22030-7404 - United States

Status: NOT_YET_RECRUITING

Clinical Research Site

Ciudad Autónoma Buenos Aires, Buenos Aires B1629AHJ - Argentina

Status: NOT_YET_RECRUITING

Clinical Research Site

Córdoba, X5004 ASL - Argentina

Status: NOT_YET_RECRUITING

Clinical Research Site

North Adelaide, South Australia 5006 - Australia

Status: NOT_YET_RECRUITING

Clinical Research Site

Parkville, Victoria 3052 - Australia

Status: NOT_YET_RECRUITING

Clinical Research Site

Porto Alegre, Rio Grande Do Sul 90560-030 - Brazil

Status: NOT_YET_RECRUITING

Clinical Research Site

Curitiba, - Brazil

Status: NOT_YET_RECRUITING

Clinical Research Site

Rio De Janeiro, 22250-020 - Brazil

Status: NOT_YET_RECRUITING

Clinical Research Site

Calgary, Alberta T3B 6A8 - Canada

Status: NOT_YET_RECRUITING

And 17 more locations available. Contact us to find the nearest participating site.

How to Enroll in This Study

To learn more about participating in this PHASE3 clinical trial for Niemann-Pick Type C Disease:

  1. Review the eligibility criteria with your healthcare provider
  2. Contact the study team for a pre-screening interview
  3. Schedule an in-person screening visit if eligible
  4. Review and sign the informed consent form
  5. Begin participation in the clinical trial

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