Patient Guide: A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis

We'll Help You Connect with This Trial

Quri.ai is a free clinical trial matching service. We help patients like you connect directly with research sites conducting this study.

  • ✓ Get matched to the right study location for you
  • ✓ Connect directly with study coordinators at 27 participating sites
  • ✓ Understand eligibility with our simplified screening tool
  • ✓ Free service - we're here to help you access clinical research
Trial ID: NCTNCT07082543
Status: 🟢 Enrolling Now
Condition: Gangliosidoses, GM2, Gangliosidosis, GM1
Phase: Phase III

Find a Study Location Near You

This study is available at 27 research sites. We'll help you connect with the location that's right for you.

Participating sites include:
  • • Oakland, California
  • • Minneapolis, Minnesota
  • • Rochester, Minnesota
  • • And 24 more locations - let us help you find the closest one

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A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis - Join Clinical Trial NCTNCT07082543

How to Join This Clinical Trial - NCTNCT07082543

Learn how to participate in this Phase III trial studying an investigational therapy for Gangliosidoses, GM2, Gangliosidosis, GM1. This study is currently enrolling participants.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Gangliosidoses, GM2, Gangliosidosis, GM1. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied
Gangliosidoses, GM2, Gangliosidosis, GM1
Treatment Being Tested
Investigational treatment
Study Phase
Phase III - Large-scale efficacy study
Enrollment Status
Currently enrolling participants
Study Identifier
NCTNCT07082543 - ClinicalTrials.gov Identifier
Sponsored By
Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

  • Initial screening to determine eligibility
  • Regular study visits and health assessments
  • Receiving the study treatment or placebo
  • Medical monitoring and follow-up care
  • Contributing to medical research that may help others
  • Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

  • Close medical monitoring by healthcare professionals
  • Access to potential new treatments
  • Compensation for time and travel (varies by study)
  • No-cost study-related medical care
  • The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 27 locations. Find a study site near you:

Clinical Research Site

Oakland, California 94609 - United States

Status: Contact for availability

Clinical Research Site

Minneapolis, Minnesota 55455 - United States

Status: Contact for availability

Clinical Research Site

Rochester, Minnesota 55905 - United States

Status: Contact for availability

Clinical Research Site

Dallas, Texas 75235 - United States

Status: Contact for availability

Clinical Research Site

Fairfax, Virginia 22030-7404 - United States

Status: Contact for availability

Clinical Research Site

Ciudad Autónoma Buenos Aires, Buenos Aires B1629AHJ - Argentina

Status: Contact for availability

Clinical Research Site

Córdoba, Córdoba Province X5004 ASL - Argentina

Status: Contact for availability

Clinical Research Site

North Adelaide, South Australia 5006 - Australia

Status: Contact for availability

Clinical Research Site

Rio de Janeiro, Rio de Janeiro 22250-020 - Brazil

Status: Contact for availability

Clinical Research Site

Porto Alegre, Rio Grande do Sul 90560-030 - Brazil

Status: Contact for availability

And 17 more locations available. Contact us to find the nearest participating site.

How to Enroll in This Study

To learn more about participating in this Phase III clinical trial for Gangliosidoses, GM2, Gangliosidosis, GM1:

  1. Review the eligibility criteria with your healthcare provider
  2. Contact the study team for a pre-screening interview
  3. Schedule an in-person screening visit if eligible
  4. Review and sign the informed consent form
  5. Begin participation in the clinical trial

Why Choose Quri.ai as Your Clinical Trial Matching Service

Quri.ai is a free clinical trial matching service that helps patients connect with research sites. We make it easier to:

  • Find clinical trials that match your condition
  • Get matched to the right study location near you
  • Connect directly with study coordinators
  • Understand if you qualify with simplified eligibility screening
  • Navigate the enrollment process with personalized support
  • Access new treatments through clinical research participation