Patient Guide: Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant

Why Use Quri.ai for This Trial?

  • ✓ Simplified eligibility checker - know if you qualify in minutes
  • ✓ Direct contact with study coordinators at 50 locations
  • ✓ Plain language explanations of medical terms and procedures
  • ✓ Personalized enrollment support throughout your journey
  • ✓ Free service - no hidden fees or obligations
Trial ID: NCTNCT06563895
Status: 🟢 Enrolling Now
Condition: Amyloidosis, Amyloid Cardiomyopathy, Transthyretin Amyloidosis, Cardiomyopathies, Heart Diseases, Polyneuropathies
Phase: PHASE3

Where You Can Participate

This study is available at 50 locations across the country.

Top locations include:
  • • La Jolla, California
  • • Stanford, California
  • • New Haven, Connecticut
  • • And 47 more locations

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Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant - Join Clinical Trial NCTNCT06563895

How to Join This Clinical Trial - NCTNCT06563895

Learn how to participate in this PHASE3 trial studying an investigational therapy for Amyloidosis, Amyloid Cardiomyopathy, Transthyretin Amyloidosis, Cardiomyopathies, Heart Diseases, Polyneuropathies. This study is currently enrolling participants.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Amyloidosis, Amyloid Cardiomyopathy, Transthyretin Amyloidosis, Cardiomyopathies, Heart Diseases, Polyneuropathies. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied
Amyloidosis, Amyloid Cardiomyopathy, Transthyretin Amyloidosis, Cardiomyopathies, Heart Diseases, Polyneuropathies
Treatment Being Tested
Investigational treatment
Study Phase
PHASE3 - Large-scale efficacy study
Enrollment Status
Currently enrolling participants
Study Identifier
NCTNCT06563895 - ClinicalTrials.gov Identifier
Sponsored By
Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

  • Initial screening to determine eligibility
  • Regular study visits and health assessments
  • Receiving the study treatment or placebo
  • Medical monitoring and follow-up care
  • Contributing to medical research that may help others
  • Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

  • Close medical monitoring by healthcare professionals
  • Access to potential new treatments
  • Compensation for time and travel (varies by study)
  • No-cost study-related medical care
  • The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 50 locations. Find a study site near you:

Clinical Research Site

La Jolla, California 92037 - United States

Status: RECRUITING

Clinical Research Site

Stanford, California 94305 - United States

Status: RECRUITING

Clinical Research Site

New Haven, Connecticut 06519 - United States

Status: RECRUITING

Clinical Research Site

Washington D.C., District of Columbia 20010 - United States

Status: RECRUITING

Clinical Research Site

Jacksonville, Florida 32224 - United States

Status: RECRUITING

Clinical Research Site

Atlanta, Georgia 30322 - United States

Status: RECRUITING

Clinical Research Site

Chicago, Illinois 60612 - United States

Status: RECRUITING

Clinical Research Site

Baltimore, Maryland 21201 - United States

Status: RECRUITING

Clinical Research Site

Baltimore, Maryland 21287 - United States

Status: RECRUITING

Clinical Research Site

Boston, Massachusetts 02114 - United States

Status: RECRUITING

And 40 more locations available. Contact us to find the nearest participating site.

How to Enroll in This Study

To learn more about participating in this PHASE3 clinical trial for Amyloidosis, Amyloid Cardiomyopathy, Transthyretin Amyloidosis, Cardiomyopathies, Heart Diseases, Polyneuropathies:

  1. Review the eligibility criteria with your healthcare provider
  2. Contact the study team for a pre-screening interview
  3. Schedule an in-person screening visit if eligible
  4. Review and sign the informed consent form
  5. Begin participation in the clinical trial

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