Patient Guide: Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A)

Why Use Quri.ai for This Trial?

  • ✓ Simplified eligibility checker - know if you qualify in minutes
  • ✓ Direct contact with study coordinators at 4 locations
  • ✓ Plain language explanations of medical terms and procedures
  • ✓ Personalized enrollment support throughout your journey
  • ✓ Free service - no hidden fees or obligations
Trial ID: NCTNCT06181136
Status: 🟢 Enrolling Now
Condition: Mucopolysaccharidoses, Mucopolysaccharidosis III
Phase: PHASE1, PHASE2

Where You Can Participate

This study is available at 4 locations across the country.

Top locations include:
  • • Oakland, California
  • • Iowa City, Iowa
  • • Chapel Hill, North Carolina
  • • And 1 more locations

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Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A) - Join Clinical Trial NCTNCT06181136

How to Join This Clinical Trial - NCTNCT06181136

Learn how to participate in this PHASE1, PHASE2 trial studying an investigational therapy for Mucopolysaccharidoses, Mucopolysaccharidosis III. This study is currently enrolling participants.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Mucopolysaccharidoses, Mucopolysaccharidosis III. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied
Mucopolysaccharidoses, Mucopolysaccharidosis III
Treatment Being Tested
Investigational treatment
Study Phase
PHASE1, PHASE2 - Safety and effectiveness study
Enrollment Status
Currently enrolling participants
Study Identifier
NCTNCT06181136 - ClinicalTrials.gov Identifier
Sponsored By
Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

  • Initial screening to determine eligibility
  • Regular study visits and health assessments
  • Receiving the study treatment or placebo
  • Medical monitoring and follow-up care
  • Contributing to medical research that may help others
  • Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

  • Close medical monitoring by healthcare professionals
  • Access to potential new treatments
  • Compensation for time and travel (varies by study)
  • No-cost study-related medical care
  • The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 4 locations. Find a study site near you:

Clinical Research Site

Oakland, California 94609 - United States

Status: RECRUITING

Clinical Research Site

Iowa City, Iowa 52242 - United States

Status: RECRUITING

Clinical Research Site

Chapel Hill, North Carolina 27514 - United States

Status: RECRUITING

Clinical Research Site

Houston, Texas 77030 - United States

Status: RECRUITING

How to Enroll in This Study

To learn more about participating in this PHASE1, PHASE2 clinical trial for Mucopolysaccharidoses, Mucopolysaccharidosis III:

  1. Review the eligibility criteria with your healthcare provider
  2. Contact the study team for a pre-screening interview
  3. Schedule an in-person screening visit if eligible
  4. Review and sign the informed consent form
  5. Begin participation in the clinical trial

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