A Natural History Study in Participants With Congenital Myasthenic Syndromes (CMS) Due to Mutations in DOK7, MUSK, AGRN, or LRP4 - Join Clinical Trial NCTNCT06078553
How to Join This Clinical Trial - NCTNCT06078553
Learn how to participate in this Not Specified trial studying an investigational therapy for Congenital Myasthenic Syndrome. This study is currently enrolling participants.
Am I Eligible for This Clinical Trial?
This clinical research study is looking for participants with Congenital Myasthenic Syndrome. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.
- Condition Being Studied
- Congenital Myasthenic Syndrome
- Treatment Being Tested
- Investigational treatment
- Study Phase
- Not Specified - Research study
- Enrollment Status
- Currently enrolling participants
- Study Identifier
- NCTNCT06078553 - ClinicalTrials.gov Identifier
- Sponsored By
- Study sponsor
What to Expect as a Participant
Participating in this clinical trial involves:
- Initial screening to determine eligibility
- Regular study visits and health assessments
- Receiving the study treatment or placebo
- Medical monitoring and follow-up care
- Contributing to medical research that may help others
- Potential access to new treatments before they're widely available
Clinical Trial Benefits and Compensation
Participants in this clinical research study may receive:
- Close medical monitoring by healthcare professionals
- Access to potential new treatments
- Compensation for time and travel (varies by study)
- No-cost study-related medical care
- The opportunity to help advance medical knowledge
Where Is This Clinical Trial Located?
This study is enrolling participants at 11 locations. Find a study site near you:
Clinical Research Site
Sacramento, California 95816 - United States
Status: RECRUITING
Clinical Research Site
Chicago, Illinois 60611 - United States
Status: RECRUITING
Clinical Research Site
O'Fallon, Illinois 62269 - United States
Status: RECRUITING
Clinical Research Site
Vienna, 1090 - Austria
Status: RECRUITING
Clinical Research Site
Ottawa, K1Y 4E9 - Canada
Status: RECRUITING
Clinical Research Site
Marseille, 13385 - France
Status: RECRUITING
Clinical Research Site
Paris, 75013 - France
Status: RECRUITING
Clinical Research Site
Milan, 20133 - Italy
Status: RECRUITING
Clinical Research Site
Valencia, 46026 - Spain
Status: RECRUITING
Clinical Research Site
Dundonald, BT16 1RH - United Kingdom
Status: RECRUITING
And 1 more locations available. Contact us to find the nearest participating site.
How to Enroll in This Study
To learn more about participating in this Not Specified clinical trial for Congenital Myasthenic Syndrome:
- Review the eligibility criteria with your healthcare provider
- Contact the study team for a pre-screening interview
- Schedule an in-person screening visit if eligible
- Review and sign the informed consent form
- Begin participation in the clinical trial
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