Patient Guide: A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)

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✓ Understand eligibility with our simplified screening tool
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Trial ID: NCTNCT05876780

Status: ACTIVE_NOT_RECRUITING

Condition: Limb Girdle Muscular Dystrophy

Phase: PHASE1

Find a Study Location Near You

This study is available at 2 research sites. We'll help you connect with the location that's right for you.

Participating sites include:

• Columbus, Ohio
• Memphis, Tennessee

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A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency) - Join Clinical Trial NCTNCT05876780

How to Join This Clinical Trial - NCTNCT05876780

Learn how to participate in this PHASE1 trial studying an investigational therapy for Limb Girdle Muscular Dystrophy. Current status: ACTIVE_NOT_RECRUITING.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Limb Girdle Muscular Dystrophy. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied: Limb Girdle Muscular Dystrophy
Treatment Being Tested: Investigational treatment
Study Phase: PHASE1 - Early safety study
Enrollment Status: ACTIVE_NOT_RECRUITING
Study Identifier: NCTNCT05876780 - ClinicalTrials.gov Identifier
Sponsored By: Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

Initial screening to determine eligibility
Regular study visits and health assessments
Receiving the study treatment or placebo
Medical monitoring and follow-up care
Contributing to medical research that may help others
Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

Close medical monitoring by healthcare professionals
Access to potential new treatments
Compensation for time and travel (varies by study)
No-cost study-related medical care
The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 2 locations. Find a study site near you:

Clinical Research Site

Columbus, Ohio 43205 - United States

Status: Contact for availability

Clinical Research Site

Memphis, Tennessee 38105 - United States

Status: Contact for availability

How to Enroll in This Study

To learn more about participating in this PHASE1 clinical trial for Limb Girdle Muscular Dystrophy:

Review the eligibility criteria with your healthcare provider
Contact the study team for a pre-screening interview
Schedule an in-person screening visit if eligible
Review and sign the informed consent form
Begin participation in the clinical trial

Why Choose Quri.ai as Your Clinical Trial Matching Service

Quri.ai is a free clinical trial matching service that helps patients connect with research sites. We make it easier to:

Find clinical trials that match your condition
Get matched to the right study location near you
Connect directly with study coordinators
Understand if you qualify with simplified eligibility screening
Navigate the enrollment process with personalized support
Access new treatments through clinical research participation