Patient Guide: A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

Why Use Quri.ai for This Trial?

  • ✓ Simplified eligibility checker - know if you qualify in minutes
  • ✓ Direct contact with study coordinators at 19 locations
  • ✓ Plain language explanations of medical terms and procedures
  • ✓ Personalized enrollment support throughout your journey
  • ✓ Free service - no hidden fees or obligations
Trial ID: NCTNCT05861999
Status: 🟢 Enrolling Now
Condition: Muscular Atrophy, Spinal
Phase: PHASE4

Where You Can Participate

This study is available at 19 locations across the country.

Top locations include:
  • • Little Rock, Arkansas
  • • Madera, California
  • • Palo Alto, California
  • • And 16 more locations

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A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy - Join Clinical Trial NCTNCT05861999

How to Join This Clinical Trial - NCTNCT05861999

Learn how to participate in this PHASE4 trial studying an investigational therapy for Muscular Atrophy, Spinal. This study is currently enrolling participants.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Muscular Atrophy, Spinal. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied
Muscular Atrophy, Spinal
Treatment Being Tested
Investigational treatment
Study Phase
PHASE4 - Research study
Enrollment Status
Currently enrolling participants
Study Identifier
NCTNCT05861999 - ClinicalTrials.gov Identifier
Sponsored By
Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

  • Initial screening to determine eligibility
  • Regular study visits and health assessments
  • Receiving the study treatment or placebo
  • Medical monitoring and follow-up care
  • Contributing to medical research that may help others
  • Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

  • Close medical monitoring by healthcare professionals
  • Access to potential new treatments
  • Compensation for time and travel (varies by study)
  • No-cost study-related medical care
  • The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 19 locations. Find a study site near you:

Clinical Research Site

Little Rock, Arkansas 72103 - United States

Status: RECRUITING

Clinical Research Site

Madera, California 93636 - United States

Status: RECRUITING

Clinical Research Site

Palo Alto, California 94304 - United States

Status: RECRUITING

Clinical Research Site

Aurora, Colorado 80045 - United States

Status: RECRUITING

Clinical Research Site

Gainesville, Florida 32610 - United States

Status: RECRUITING

Clinical Research Site

Atlanta, Georgia 30329-2309 - United States

Status: RECRUITING

Clinical Research Site

Grand Rapids, Michigan 49503 - United States

Status: RECRUITING

Clinical Research Site

Philadelphia, Pennsylvania 19104 - United States

Status: RECRUITING

Clinical Research Site

Dallas, Texas 75390 - United States

Status: RECRUITING

Clinical Research Site

Norfolk, Virginia 23510 - United States

Status: RECRUITING

And 9 more locations available. Contact us to find the nearest participating site.

How to Enroll in This Study

To learn more about participating in this PHASE4 clinical trial for Muscular Atrophy, Spinal:

  1. Review the eligibility criteria with your healthcare provider
  2. Contact the study team for a pre-screening interview
  3. Schedule an in-person screening visit if eligible
  4. Review and sign the informed consent form
  5. Begin participation in the clinical trial

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