Patient Guide: A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

Why Use Quri.ai for This Trial?

  • ✓ Simplified eligibility checker - know if you qualify in minutes
  • ✓ Direct contact with study coordinators at 16 locations
  • ✓ Plain language explanations of medical terms and procedures
  • ✓ Personalized enrollment support throughout your journey
  • ✓ Free service - no hidden fees or obligations
Trial ID: NCTNCT05861986
Status: 🟢 Enrolling Now
Condition: Muscular Atrophy, Spinal
Phase: PHASE4

Where You Can Participate

This study is available at 16 locations across the country.

Top locations include:
  • • Little Rock, Arkansas
  • • Aurora, Colorado
  • • Gainesville, Florida
  • • And 13 more locations

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A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy - Join Clinical Trial NCTNCT05861986

How to Join This Clinical Trial - NCTNCT05861986

Learn how to participate in this PHASE4 trial studying an investigational therapy for Muscular Atrophy, Spinal. This study is currently enrolling participants.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Muscular Atrophy, Spinal. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied
Muscular Atrophy, Spinal
Treatment Being Tested
Investigational treatment
Study Phase
PHASE4 - Research study
Enrollment Status
Currently enrolling participants
Study Identifier
NCTNCT05861986 - ClinicalTrials.gov Identifier
Sponsored By
Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

  • Initial screening to determine eligibility
  • Regular study visits and health assessments
  • Receiving the study treatment or placebo
  • Medical monitoring and follow-up care
  • Contributing to medical research that may help others
  • Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

  • Close medical monitoring by healthcare professionals
  • Access to potential new treatments
  • Compensation for time and travel (varies by study)
  • No-cost study-related medical care
  • The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 16 locations. Find a study site near you:

Clinical Research Site

Little Rock, Arkansas 72103 - United States

Status: RECRUITING

Clinical Research Site

Aurora, Colorado 80045 - United States

Status: RECRUITING

Clinical Research Site

Gainesville, Florida 32610 - United States

Status: RECRUITING

Clinical Research Site

Atlanta, Georgia 30329-2309 - United States

Status: RECRUITING

Clinical Research Site

Chicago, Illinois 60611 - United States

Status: NOT_YET_RECRUITING

Clinical Research Site

Grand Rapids, Michigan 49503 - United States

Status: RECRUITING

Clinical Research Site

New York, New York 10032 - United States

Status: RECRUITING

Clinical Research Site

Philadelphia, Pennsylvania 19104 - United States

Status: RECRUITING

Clinical Research Site

Dallas, Texas 75390 - United States

Status: RECRUITING

Clinical Research Site

Fort Worth, Texas 76104 - United States

Status: RECRUITING

And 6 more locations available. Contact us to find the nearest participating site.

How to Enroll in This Study

To learn more about participating in this PHASE4 clinical trial for Muscular Atrophy, Spinal:

  1. Review the eligibility criteria with your healthcare provider
  2. Contact the study team for a pre-screening interview
  3. Schedule an in-person screening visit if eligible
  4. Review and sign the informed consent form
  5. Begin participation in the clinical trial

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