Patient Guide: Long-term Follow-up Study of Risdiplam in Participants With Spinal Muscular Atrophy (SMA)

Why Use Quri.ai for This Trial?

  • ✓ Simplified eligibility checker - know if you qualify in minutes
  • ✓ Direct contact with study coordinators at 39 locations
  • ✓ Plain language explanations of medical terms and procedures
  • ✓ Personalized enrollment support throughout your journey
  • ✓ Free service - no hidden fees or obligations
Trial ID: NCTNCT05232929
Status: ACTIVE_NOT_RECRUITING
Condition: Spinal Muscular Atrophy
Phase: PHASE4

Where You Can Participate

This study is available at 39 locations across the country.

Top locations include:
  • • Phoenix, Arizona
  • • Phoenix, Arizona
  • • Little Rock, Arkansas
  • • And 36 more locations

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Long-term Follow-up Study of Risdiplam in Participants With Spinal Muscular Atrophy (SMA) - Join Clinical Trial NCTNCT05232929

How to Join This Clinical Trial - NCTNCT05232929

Learn how to participate in this PHASE4 trial studying an investigational therapy for Spinal Muscular Atrophy. Current status: ACTIVE_NOT_RECRUITING.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Spinal Muscular Atrophy. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied
Spinal Muscular Atrophy
Treatment Being Tested
Investigational treatment
Study Phase
PHASE4 - Research study
Enrollment Status
ACTIVE_NOT_RECRUITING
Study Identifier
NCTNCT05232929 - ClinicalTrials.gov Identifier
Sponsored By
Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

  • Initial screening to determine eligibility
  • Regular study visits and health assessments
  • Receiving the study treatment or placebo
  • Medical monitoring and follow-up care
  • Contributing to medical research that may help others
  • Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

  • Close medical monitoring by healthcare professionals
  • Access to potential new treatments
  • Compensation for time and travel (varies by study)
  • No-cost study-related medical care
  • The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 39 locations. Find a study site near you:

Clinical Research Site

Phoenix, Arizona 85013 - United States

Status: Contact for availability

Clinical Research Site

Phoenix, Arizona 85016 - United States

Status: Contact for availability

Clinical Research Site

Little Rock, Arkansas 72103 - United States

Status: Contact for availability

Clinical Research Site

Loma Linda, California 92354 - United States

Status: Contact for availability

Clinical Research Site

Los Angeles, California 90010 - United States

Status: Contact for availability

Clinical Research Site

Madera, California 93636 - United States

Status: Contact for availability

Clinical Research Site

Orange, California 92868 - United States

Status: Contact for availability

Clinical Research Site

Sacramento, California 95817 - United States

Status: Contact for availability

Clinical Research Site

Aurora, Colorado 80045 - United States

Status: Contact for availability

Clinical Research Site

Washington D.C., District of Columbia 20007 - United States

Status: Contact for availability

And 29 more locations available. Contact us to find the nearest participating site.

How to Enroll in This Study

To learn more about participating in this PHASE4 clinical trial for Spinal Muscular Atrophy:

  1. Review the eligibility criteria with your healthcare provider
  2. Contact the study team for a pre-screening interview
  3. Schedule an in-person screening visit if eligible
  4. Review and sign the informed consent form
  5. Begin participation in the clinical trial

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