Patient Guide: A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C

Why Use Quri.ai for This Trial?

  • ✓ Simplified eligibility checker - know if you qualify in minutes
  • ✓ Direct contact with study coordinators at 14 locations
  • ✓ Plain language explanations of medical terms and procedures
  • ✓ Personalized enrollment support throughout your journey
  • ✓ Free service - no hidden fees or obligations
Trial ID: NCTNCT05163288
Status: 🟢 Enrolling Now
Condition: Niemann-Pick Disease, Type C
Phase: PHASE3

Where You Can Participate

This study is available at 14 locations across the country.

Top locations include:
  • • Rochester, Minnesota
  • • Parkville, Victoria
  • • Praha,
  • • And 11 more locations

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A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C - Join Clinical Trial NCTNCT05163288

How to Join This Clinical Trial - NCTNCT05163288

Learn how to participate in this PHASE3 trial studying an investigational therapy for Niemann-Pick Disease, Type C. This study is currently enrolling participants.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Niemann-Pick Disease, Type C. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied
Niemann-Pick Disease, Type C
Treatment Being Tested
Investigational treatment
Study Phase
PHASE3 - Large-scale efficacy study
Enrollment Status
Currently enrolling participants
Study Identifier
NCTNCT05163288 - ClinicalTrials.gov Identifier
Sponsored By
Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

  • Initial screening to determine eligibility
  • Regular study visits and health assessments
  • Receiving the study treatment or placebo
  • Medical monitoring and follow-up care
  • Contributing to medical research that may help others
  • Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

  • Close medical monitoring by healthcare professionals
  • Access to potential new treatments
  • Compensation for time and travel (varies by study)
  • No-cost study-related medical care
  • The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 14 locations. Find a study site near you:

Clinical Research Site

Rochester, Minnesota 55905 - United States

Status: COMPLETED

Clinical Research Site

Parkville, Victoria 3050 - Australia

Status: ACTIVE_NOT_RECRUITING

Clinical Research Site

Praha, 128 08 - Czechia

Status: ACTIVE_NOT_RECRUITING

Clinical Research Site

Gießen, 35389 - Germany

Status: ACTIVE_NOT_RECRUITING

Clinical Research Site

Hamburg, 20246 - Germany

Status: COMPLETED

Clinical Research Site

Hochheim, 65239 - Germany

Status: ACTIVE_NOT_RECRUITING

Clinical Research Site

München, 80539 - Germany

Status: NOT_YET_RECRUITING

Clinical Research Site

Münster, 48149 - Germany

Status: ACTIVE_NOT_RECRUITING

Clinical Research Site

Amsterdam, 1105 - Netherlands

Status: RECRUITING

Clinical Research Site

Bratislava, 833 40 - Slovakia

Status: ACTIVE_NOT_RECRUITING

And 4 more locations available. Contact us to find the nearest participating site.

How to Enroll in This Study

To learn more about participating in this PHASE3 clinical trial for Niemann-Pick Disease, Type C:

  1. Review the eligibility criteria with your healthcare provider
  2. Contact the study team for a pre-screening interview
  3. Schedule an in-person screening visit if eligible
  4. Review and sign the informed consent form
  5. Begin participation in the clinical trial

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