Patient Guide: A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)

Why Use Quri.ai for This Trial?

  • ✓ Simplified eligibility checker - know if you qualify in minutes
  • ✓ Direct contact with study coordinators at 75 locations
  • ✓ Plain language explanations of medical terms and procedures
  • ✓ Personalized enrollment support throughout your journey
  • ✓ Free service - no hidden fees or obligations
Trial ID: NCTNCT04770779
Status: ACTIVE_NOT_RECRUITING
Condition: Thalassemia, beta-Thalassemia, alpha-Thalassemia
Phase: PHASE3

Where You Can Participate

This study is available at 75 locations across the country.

Top locations include:
  • • Phoenix, Arizona
  • • La Jolla, California
  • • Oakland, California
  • • And 72 more locations

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A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT) - Join Clinical Trial NCTNCT04770779

How to Join This Clinical Trial - NCTNCT04770779

Learn how to participate in this PHASE3 trial studying an investigational therapy for Thalassemia, beta-Thalassemia, alpha-Thalassemia. Current status: ACTIVE_NOT_RECRUITING.

Am I Eligible for This Clinical Trial?

This clinical research study is looking for participants with Thalassemia, beta-Thalassemia, alpha-Thalassemia. Eligibility requirements include specific age ranges, health status, and medical history. Contact the study team to learn if you qualify.

Condition Being Studied
Thalassemia, beta-Thalassemia, alpha-Thalassemia
Treatment Being Tested
Investigational treatment
Study Phase
PHASE3 - Large-scale efficacy study
Enrollment Status
ACTIVE_NOT_RECRUITING
Study Identifier
NCTNCT04770779 - ClinicalTrials.gov Identifier
Sponsored By
Study sponsor

What to Expect as a Participant

Participating in this clinical trial involves:

  • Initial screening to determine eligibility
  • Regular study visits and health assessments
  • Receiving the study treatment or placebo
  • Medical monitoring and follow-up care
  • Contributing to medical research that may help others
  • Potential access to new treatments before they're widely available

Clinical Trial Benefits and Compensation

Participants in this clinical research study may receive:

  • Close medical monitoring by healthcare professionals
  • Access to potential new treatments
  • Compensation for time and travel (varies by study)
  • No-cost study-related medical care
  • The opportunity to help advance medical knowledge

Where Is This Clinical Trial Located?

This study is enrolling participants at 75 locations. Find a study site near you:

Clinical Research Site

Phoenix, Arizona 85016-7710 - United States

Status: Contact for availability

Clinical Research Site

La Jolla, California 92093 - United States

Status: Contact for availability

Clinical Research Site

Oakland, California 94609-1809 - United States

Status: Contact for availability

Clinical Research Site

Palo Alto, California 94304-1601 - United States

Status: Contact for availability

Clinical Research Site

Boston, Massachusetts 02115 - United States

Status: Contact for availability

Clinical Research Site

Detroit, Michigan 48201-2196 - United States

Status: Contact for availability

Clinical Research Site

New York, New York 10065-4870 - United States

Status: Contact for availability

Clinical Research Site

Durham, North Carolina 27710-3038 - United States

Status: Contact for availability

Clinical Research Site

Philadelphia, Pennsylvania 19104 - United States

Status: Contact for availability

Clinical Research Site

Seattle, Washington 98101 - United States

Status: Contact for availability

And 65 more locations available. Contact us to find the nearest participating site.

How to Enroll in This Study

To learn more about participating in this PHASE3 clinical trial for Thalassemia, beta-Thalassemia, alpha-Thalassemia:

  1. Review the eligibility criteria with your healthcare provider
  2. Contact the study team for a pre-screening interview
  3. Schedule an in-person screening visit if eligible
  4. Review and sign the informed consent form
  5. Begin participation in the clinical trial

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